Titre:
  • Rebalancing innovation, affordability, and access for orphan drugs in the European Union
Auteur:Stevens, Hilde; Siotis, Georges; Castanheira De Moura, Micael; Dewatripont, Mathias; Akodad, Sanaé; Daems, Sam; Fischer, Alain; Goldman, Michel
Informations sur la publication:The Lancet Regional Health - Europe, 68, 101778
Statut de publication:Publié, 2026-09
Sujet CREF:Economie
Mots-clés:Access
Affordability
Draghi Report
Drug pricing
EU Biotech Act
EU Pharma Package reform
Innovation incentives
Market exclusivity
Orphan medicinal products (OMPs)
Policy
Rare diseases
Regulation
Note générale:SCOPUS: re.j
Langue:Anglais
Identificateurs:urn:issn:2666-7762
info:doi/10.1016/j.lanepe.2026.101778
info:pii/S2666776226001900
info:scp/105046182897
RePEc:ulb:ulbeco:2013/414127