Titre:
  • Safety and efficacy of tamoxifen in non-ambulant patients with Duchenne muscular dystrophy: a multicentre, randomised, double–blind, placebo–controlled, phase 3 trial (TAMDMD Group B)
Auteur:Henzi, Bettina Cornelia; Putananickal, Niveditha; Schmidt, Simone; Nagy, Sara; Rubino–Nacht, Daniela; Schaedelin, Sabine; Amthor, Helge; Childs, Anne–Marie –M; Deconinck, Nicolas; Horrocks, Iain; Houwen–van Opstal, Saskia; Laugel, Vincent; Lobato, Mercedes Lopez; Osorio, Andrés Nascimento; Schara–Schmidt, Ulrike; Spinty, Stefan; von Moers, Arpad; Lawrence, Fiona; Hafner, Patricia; Dorchies, Olivier O.M.; Fischer, Dirk
Informations sur la publication:Neuromuscular disorders, 47, 105275
Statut de publication:Publié, 2025-02
Sujet CREF:Neurologie
Pédiatrie
Génétique clinique
Mots-clés:Corticosteroid naive
Duchenne muscular dystrophy
Motor function measurement
Non-ambulant duchenne muscular dystrophy
Tamoxifen
Note générale:SCOPUS: ar.j
Langue:Anglais
Identificateurs:urn:issn:0960-8966
info:doi/10.1016/j.nmd.2025.105275
info:pii/S0960896625000021
info:scp/85216105139
info:pmid/39879732