Titre:
  • Lentivirus-mediated gene therapy corrects ribosomal biogenesis and shows promise for Diamond Blackfan anemia
Auteur:Giménez, Yari; Palacios, Manuel; Sánchez-Domínguez, Rebeca; Zorbas, Christiane; Peral, Jorge; Puzik, Alexander; Ugalde, Laura; Alberquilla, Omaira; Villanueva, Mariela; Río, Paula; Gálvez, Eva; Da Costa, Lydie L.M.; Strullu, Marion; Catala, Albert; Ruiz-Llobet, Anna; Segovia, Jose Carlos; Sevilla, Julián; Strahm, Brigitte; Niemeyer, Charlotte Marie; Belendez, Cristina; Leblanc, Thierry; Lafontaine, Denis; Bueren, Juan; Navarro, Susana
Informations sur la publication:JCI insight, 9, 10, e171650
Statut de publication:Publié, 2024-05-01
Sujet CREF:Généralités
Note générale:SCOPUS: ar.j
Langue:Anglais
Identificateurs:urn:issn:2379-3708
info:doi/10.1172/jci.insight.171650
info:scp/85194022095
info:pmid/38775150