Titre:
  • Therapeutic benefit of idebenone in patients with Leber hereditary optic neuropathy: The LEROS nonrandomized controlled trial
Auteur:Yu-Wai-Man, Patrick; Carelli, Valerio; Newman, Nancy N.J.; Silva, Magda Joana; Linden, Aki; Van Stavern, Gregory G.P.; Szaflik, Jacek Paweł; Banik, Rudrani; Lubiński, Wojciech; Pemp, Berthold; Liao, Yaping Joyce; Subramanian, Prem P.S.; Misiuk-Hojło, Marta; Newman, Steven; Castillo, Lorena; Kocięcki, Jarosław; Levin, Marc M.H.; Muñoz-Negrete, Francisco Jose; Yagan, Ali; Cherninkova, Sylvia; Katz, David; Meunier, Audrey; Votruba, Marcela; Korwin, Magdalena; Dziedziak, Jacek; Jurkute, Neringa; Harvey, Joshua Paul; La Morgia, Chiara; Priglinger, Claudia; Llòria, Xavier; Tomasso, Livia; Klopstock, Thomas
Informations sur la publication:Cell Reports Medicine, 5, 3, 101437
Statut de publication:Publié, 2024-03
Sujet CREF:Généralités
Mots-clés:idebenone
Leber hereditary optic neuropathy
LHON
mitochondrial disease
mtDNA
neuro-ophthalmology
optic atrophy
optic neuropathy
retinal ganglion cells
Note générale:SCOPUS: ar.j
Langue:Anglais
Identificateurs:urn:issn:2666-3791
info:doi/10.1016/j.xcrm.2024.101437
info:pii/S2666379124000600
info:scp/85186340511
info:pmid/38428428