Titre:
  • A phase 3 randomized placebo-controlled trial of tadalafil for Duchenne muscular dystrophy.
Auteur:Victor, Ronald G; Sweeney, Lee HL; Finkel, Richard RS; Deconinck, Nicolas; Byrne, Barry; Eagle, Michelle; Goemans, Nathalie; Vandenborne, Krista; Dubrovsky, Alberto AL; Topaloglu, Haluk; Miceli, Carrie MC; Furlong, Pat; Landry, John; Elashoff, Robert; Cox, David A.; Tadalafil DMD Study Group,
Informations sur la publication:Neurology, 89, 17, page (1811-1820)
Statut de publication:Publié, 2017-10
Sujet CREF:Sciences bio-médicales et agricoles
MeSH keywords:Adolescent
Area Under Curve
Child
Dose-Response Relationship, Drug
Double-Blind Method
Follow-Up Studies
Glucocorticoids -- therapeutic use
Heart Rate -- physiology
Humans
International Cooperation
Male
Muscular Dystrophy, Duchenne -- drug therapy -- psychology
Quality of Life
Respiratory Function Tests
Tadalafil -- therapeutic use
Treatment Outcome
Vasodilator Agents -- therapeutic use
Ventricular Function, Left
Walking -- physiology
Langue:Anglais
Identificateurs:urn:issn:0028-3878
info:doi/10.1212/WNL.0000000000004570
info:pii/WNL.0000000000004570
info:pmid/28972192
PMC5664308