par Versteegh, C;Avni, Efraim ;Cuvelier, Philippe ;Ferster, Alina
Référence Archives de pédiatrie, 5, 12, page (1341-1343)
Publication Publié, 1998-12
Référence Archives de pédiatrie, 5, 12, page (1341-1343)
Publication Publié, 1998-12
Article révisé par les pairs
Résumé : | Gaucher's disease is a serious disorder which becomes curable by bone marrow transplantation. Enzyme replacement therapy has permitted improvement in quality of life and has been shown to decrease the disease's progression. |