Titre:
  • Gene therapy for immunodeficiency due to adenosine deaminase deficiency.
Auteur:Aiuti, Alessandro; Cattaneo, Federica; Galimberti, Stefania; Benninghoff, Ulrike; Cassani, Barbara; Callegaro, Luciano; Scaramuzza, Samantha; Andolfi, Grazia; Mirolo, Massimiliano; Brigida, Immacolata; Tabucchi, Antonella; Carlucci, Filippo; Eibl, Martha; Aker, Memet; Slavin, Shimon; Al-Mousa, Hamoud; Al Ghonaium, Abdulaziz; Ferster, Alina; Duppenthaler, Andrea; Notarangelo, Luigi; Wintergerst, Uwe; Buckley, Rebecca H; Bregni, Marco; Marktel, Sarah; Valsecchi, Maria Grazia; Rossi, Pier Luca; Ciceri, Fabio; Miniero, Roberto; Bordignon, Claudio; Roncarolo, Maria-Grazia
Informations sur la publication:The New England journal of medicine, 360, 5, page (447-458)
Statut de publication:Publié, 2009-01
Sujet CREF:Pédiatrie
Cancérologie
Hématologie
MeSH keywords:Transplantation Conditioning
Note générale:Clinical Trial, Phase I
Clinical Trial, Phase II
Journal Article
Multicenter Study
Research Support, Non-U.S. Gov't
SCOPUS: ar.j
Langue:Anglais
Identificateurs:urn:issn:0028-4793
info:doi/10.1056/NEJMoa0805817
info:pii/360/5/447
info:scp/59449098985
info:pmid/19179314