Titre:
  • Phase 3 Trial of Inhaled Molgramostim in Autoimmune Pulmonary Alveolar Proteinosis.
Auteur:Trapnell, Bruce BC; Inoue, Yoshikazu; Bonella, Francesco; Wang, Tisha; Mc Carthy, Chloé; Arai, T.; Akasaka, Keiichi; Mariani, Francesca; Mogulkoc, Nesrin; Song, Jin Woo; Bondue, Benjamin; Jouneau, Stéphane; Numakura, Tadahisa; Öcal, Nesrin; Mihaltan, Florin; Ataya, Ali; Bendstrup, Elisabeth; Campo, Ilaria; Carey, Brenna; Arena, Ross; Robinson, Baudry; Fleming, Richard; Wasfi, Yasmine; Pratt, Raymond; IMPALA-2 Trial Investigators,
Informations sur la publication:The New England journal of medicine, 393, 8, page (764-773)
Statut de publication:Publié, 2025-08-01
Sujet CREF:Sciences bio-médicales et agricoles
MeSH keywords:Adult
Female
Humans
Male
Middle Aged
Administration, Inhalation
Autoimmune Diseases -- diagnosis -- drug therapy -- immunology -- physiopathology
Double-Blind Method
Granulocyte-Macrophage Colony-Stimulating Factor -- administration & dosage -- adverse effects
Pulmonary Alveolar Proteinosis -- diagnosis -- drug therapy -- immunology -- physiopathology
Pulmonary Diffusing Capacity -- drug effects -- physiology
Quality of Life
Recombinant Proteins -- administration & dosage -- adverse effects
Severity of Illness Index
Langue:Anglais
Identificateurs:urn:issn:0028-4793
info:doi/10.1056/NEJMoa2410542
info:pmid/40834301