Article révisé par les pairs
Titre:
  • Efficacy and Safety of Leriglitazone in Patients with Friedreich Ataxia: A Phase 2 Double-Blind, Randomized Controlled Trial (FRAMES)
Auteur:Pandolfo, Massimo; Reetz, Kathrin; Darling, Alejandra; Rodriguez De Rivera, Francisco Javier; Henry, Pierre Gilles; Joers, James; Lenglet, Christophe; Adanyeguh, Isaac; Deelchand, Dinesh; Mochel, Fanny; Pousset, Francoise; Pascual, Sílvia; Van Den Eede, Delphine; Martin-Ugarte, Itziar; Vilà-Brau, Anna; Mantilla, Adriana; Pascual, María; Martinell, Marc; Meya, Uwe; Durr, Alexandra
Informations sur la publication:Neurology: Genetics, 8, 6, e200034
Statut de publication:Publié, 2022-12
Sujet CREF:Neurologie
Note générale:SCOPUS: ar.j
DecretOANoAutActif
Langue:Anglais
Identificateurs:urn:issn:2376-7839
info:doi/10.1212/NXG.0000000000200034
info:scp/85143821367

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