Functional trajectories before and after loss of ambulation in Duchenne muscular dystrophy and implications for clinical trials
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McDonald, CRAIG C.M.
, Signorovitch, James
, Mercuri, Eugenio Maria E.
, Niks, Erik E.H.
, Wong, Brenda BL
, Fillbrunn, Mirko
, Sajeev, Gautam
, Yim, Erica
, Dieye, Ibrahima
, Miller, Debra
, Ward, Susan S.J.
, Goemans, Nathalie
, Deconinck, Nicolas
, Tulinius, Már
, de Groot, Imelda
, Flanigan, Kevin
, de Resende, Maria Bernadete Dutra
, Vita, Gianluca
, Schara, Ulrike
, Kirschner, Janbernd
, Topaloglu, Haluk
, Monges, Soledad
, Cances, Claude
Publication
2024-06