Titre:
  • Baboon envelope pseudotyped lentiviral vectors efficiently transduce human B cells and allow active factor IX B cell secretion in vivo in NOD/SCIDγc-/- mice
Auteur:Levy, Camille; Nair, Nisha; VandenDriessche, Thierry; Chuah Lay Khim, Marinee; Cosset, François-Loïc; Verhoeyen, Els; Fusil, Floriane; Amirache, Fouzia; Costa, Caroline; Girard-Gagnepain, Anaïs; Negre, Didier; Bernadin, Ornellie; Garaulet, Guillermo; Rodriguez, Antonio
Informations sur la publication:Journal of thrombosis and haemostasis, 14, 12, page (2478-2492)
Statut de publication:Publié, 2016-12
Sujet CREF:Hématologie
Mots-clés:b cells
factor IX
gene therapy
hemophilia
lentiviral vector
Note générale:SCOPUS: ar.j
FLWNA
Langue:Anglais
Identificateurs:urn:issn:1538-7933
info:doi/10.1111/jth.13520
info:scp/84997795132